Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...

Some genetic disorders—such as cystic fibrosis, hemophilia and Tay Sachs disease—involve many mutations in a person's genome, ...

Liver cells are indispensable for research—for drug testing, to better understand diseases such as hepatitis, fatty liver, cirrhosis, or liver cancer and for development of future cell therapies.

Scientists at The University of Texas at Austin have developed a revolutionary gene-editing method using bacterial retrons ...

An increasing demand for gene therapies is focusing the industry on enhancing production capabilities, transitioning from ...

Traditional breeding and genetic modification methods have struggled to keep pace with the rapid evolution of plant viruses. CRISPR/Cas systems, originally derived from bacterial immune responses, ...

Some gene therapy treatments use modified adeno-associated viruses (AAVs) like the one shown here to deliver therapeutic genetic material into a patient’s cells. In a finding with implications for one ...

Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...

For many diseases and chronic conditions, an individual's genes play a role in their likelihood of developing the disease. While some inherited diseases, such as cystic fibrosis or sickle cell anemia, ...

Canada is ready for the next genetic revolution. Farmers like me applaud the Canadian Food Inspection Agency (CFIA) for letting sound science guide agricultural policy—and clearing up the ...