The U.S. government is divesting from mRNA vaccines, but will other uses of the technology be spared? In a time of ...

A Florida girl was born with a rare genetic disease. Her parents have been treating her with a medicine, but the FDA recently ...

An international research team, led by Shinghua Ding at the University of Missouri, has identified a previously unknown ...

A University of Missouri-led discovery could pave the way for improved diagnosis and treatment of unexplained movement ...

Paige Headland, from Thornaby, was born with severe medical issues and it took years for her to be diagnosed with CTNNB1 ...

In 1962, a pediatric neurology resident at Columbia's Neurological Institute and his colleagues in the College of Physicians ...

PUDUKOTTAI: The Pudukottai District Consumer Disputes Redressal Commission on Wednesday ordered a private hospital in ...

You wouldn't know it watching Lilly Lou go through life with her independence, spirit, strong will, mobility, kindness, ...

After Rachel Johnson’s daughter was diagnosed with PWS, she worried about what would happen during the candy-centered holiday ...

BridgeBio Pharma's experimental drug for a rare genetic condition that causes low blood calcium met all the main and secondary goals in a late-stage study, the company said on Wednesday.

Emma Suetta, an 11-year-old from Greenview, was recognized at the American Kidney Fund’s annual Hope Affair in Washington, ...

Because the new method can replace a large stretch of defective DNA with a healthy sequence, the same retron-based package can fix any combination of mutations within that stretch of DNA without ...